Rocket Pharmaceuticals Inc is a pioneering biotechnology firm dedicated to developing gene therapies for rare and severe diseases. With a focus on late-stage research, the company is advancing treatments for conditions like fanconi anemia, leukocyte adhesion deficiency-I, and pyruvate kinase deficiency, all of which impact blood cell production or function. Additionally, Rocket Pharmaceuticals is working on gene therapies for Danon disease and various cardiac disorders, leveraging partnerships with research institutions and leveraging cutting-edge technology to address unmet medical needs. Founded in 1999, Rocket Pharmaceuticals is headquartered in Cranbury, New Jersey.

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